Amicus Therapeutics Announces Upcoming Presentations at the American Society of Gene & Cell Therapy 24th Annual Meeting

Rhea-AI Summary

Amicus Therapeutics (Nasdaq: FOLD) has announced the acceptance of two abstracts for the American Society of Gene & Cell Therapy 24th Annual Meeting, occurring virtually from May 11-14, 2021. The presentations will feature preclinical data from the company's gene therapy programs targeting Fabry and Pompe diseases. The Pompe disease abstract, presented by Ali Ramezani, focuses on muscle pathology reversal, while the Fabry disease abstract, by CJ Song, discusses the efficacy of a new transgene. These insights underscore Amicus's commitment to rare metabolic diseases.

PHILADELPHIA, May 05, 2021 (GLOBE NEWSWIRE) -- Amicus Therapeutics (Nasdaq: FOLD), today announced the acceptance of two abstracts for presentation at the American Society of Gene & Cell Therapy 24th Annual Meeting being held virtually, May 11-14, 2021. Accepted abstracts will highlight preclinical data from the Company’s Fabry and Pompe gene therapy programs, which Amicus is developing with the Gene Therapy Program of the Perelman School of Medicine at the University of Pennsylvania.

Digital Poster Session: Tuesday, May 11, 8:00 - 10:00 a.m. ET

Pompe Disease:

• Title: Post-Symptomatic Reversal of Muscle Pathology in a Model of Pompe Disease Using Gene Therapy
• Session title: Metabolic, Storage, Endocrine, Liver and Gastrointestinal Diseases
• Abstract number: 518
• Presenter: Ali Ramezani, Ph.D., Senior Research Investigator, Project Lead, Translational Research, Gene Therapy Program, University of Pennsylvania

Fabry Disease:

• Title: Efficacy of Adeno-Associated Viruses Expressing an Engineered Alpha-Galactosidase A Transgene in a Mouse Model of Fabry Disease
• Session title: Metabolic, Storage, Endocrine, Liver and Gastrointestinal Diseases
• Abstract number: 519
• Presenter: CJ (Chunjuan) Song, Ph.D., DABT, Research Director, Translational Research, Gene Therapy Program, University of Pennsylvania

The posters will be made available on the Amicus website following their respective presentations at the meeting.

For more information on the American Society of Gene & Cell Therapy 24^th Annual Meeting, please visit https://annualmeeting.asgct.org/.

About Amicus Therapeutics
Amicus Therapeutics (Nasdaq: FOLD) is a global, patient-dedicated biotechnology company focused on discovering, developing and delivering novel high-quality medicines for people living with rare metabolic diseases. With extraordinary patient focus, Amicus Therapeutics is committed to advancing and expanding a robust pipeline of cutting-edge, first- or best-in-class medicines for rare metabolic diseases. For more information please visit the company’s website at www.amicusrx.com, and follow us on Twitter and LinkedIn.

CONTACT:

Investors:
Andrew Faughnan
Sr. Director, Investor Relations
afaughnan@amicusrx.com
(609) 662-3809

Media:
Diana Moore
Head of Global Corporate Communications
dmoore@amicusrx.com
(609) 662-5079

FOLD–G

FAQ

What abstracts were accepted for Amicus Therapeutics at the ASGCT Annual Meeting?

Amicus Therapeutics has two abstracts accepted, focusing on their gene therapy programs for Fabry and Pompe diseases.

When is the ASGCT Annual Meeting where Amicus will present?

The ASGCT Annual Meeting is scheduled for May 11-14, 2021.

Who is presenting the Pompe disease abstract for Amicus Therapeutics?

The Pompe disease abstract will be presented by Ali Ramezani, Ph.D.

What is the title of the Fabry disease abstract presented by Amicus?

The title of the Fabry disease abstract is 'Efficacy of Adeno-Associated Viruses Expressing an Engineered Alpha-Galactosidase A Transgene in a Mouse Model of Fabry Disease'.

Where can I find more information about the presentations from Amicus Therapeutics?

The posters will be available on the Amicus Therapeutics website following their presentations at the meeting.